👉 Sons Research, a biotech company based in Austin, Texas, focuses on developing innovative therapeutic solutions for rare genetic diseases through gene editing and personalized medicine. Their groundbreaking research involves using CRISPR-Cas9 technology to precisely edit genes, aiming to correct mutations at their source. By targeting specific genetic defects, Sons seeks to create treatments that not only alleviate symptoms but also address the root causes of diseases like spinal muscular atrophy and certain forms of inherited blindness. The company emphasizes a patient-centric approach, collaborating closely with clinicians and patients to tailor therapies that maximize efficacy and minimize side effects, thereby advancing the field of gene therapy and offering hope for conditions with limited treatment options.